Stem Cell Applications
Complete List of Current Stem Cell Applications
Liposomal Storage Diseases
- Adrenoleukodystrophy
- Gaucher's Disease
- Hunter's Syndrome (MPS-II)
- Hurler's Syndrome (MPS-IH)
- Krabbe Disease
- Maroteaux-Lamy Syndrome (MPS-VI)
- Metachromatic Leukodystrophy
- Morquio Syndrome (MPS –IV)
- Mucolipidosis II (I-cell Disease)
- Mucopolysaccharidoses (MPS)
- Niemann-Pick Disease
- Sanfilippo Syndrome (MPS-III)
- Scheie Syndrome (MPS-IS)
- Sly Syndrome Beta-Glucuronidase Deficiency (MPS-VII)
- Wolman Disease
Acute Leukemias
- Acute Biphenotypic Leukemia
- Acute Lymphoblastic Leukemia (ALL)
- Acute Myelogenous Leukemia (AML)
- Acute Undifferentiated Leukemia
Chronic Leukemias
- Chronic Lymphocytic Leukemia (CLL)
- Chronic Myelogenous Leukemia (CML)
- Juvenile Chronic Myelogenous Leukemia (JCML)
- Juvenile Myelomonocytic Leukemia (JMML)
Lymphoproliferative Disorders
- Hodgkin’s Disease
- Non-Hodgkin’s Lymphoma
- Prolymphocytic Leukemia
Histiocytic Disorders
- Familial Erythrophagocy Lymphohistiocytosis
- Hemophagocytasis
- Histiocytosis-X
- Langerhans' Cell Histiocytosis
Inherited Red Cell (Erythrocyte) Abnormalities
- Beta Thalassemia Major (Cooley’s Anemia)
- Blackfan-Diamond Anemia
- Pure Red Cell Aplasia
- Sickle Cell Disease
Congenital (Inherited) Immune System Disorders
- Absence of T & B Cells SCID
- Absence of T Cells, Normal B Cell SCID
- Ataxia-Telangiectasia
- Bare Lymphocyte Syndrome
- Common Variable Immunodeficiency
- DiGeorge Syndrome
- Kostmann Syndrome
- Leukocyte Adhesion Deficiency
- Omenn's Syndrome
- Severe Combined Immunodeficiency (SCID)
- SCID with Adenosine Deaminase Deficiency
- Wiskott-Aldrich Syndrome
- X-Linked Lymphoproliferative Disorder
Other Inherited Disorders
- Cartilage-Hair Hypoplasia
- Ceroid Lipofuscinosis
- Congenital Erythropoietic Porphyria
- Glanzmann Thrombasthenia
- Lesch-Nyhan Syndrome
- Osteopetrosis
- Tay Sachs Disease
Myelodysplastic Syndromes
- Amyloidosis
- Chronic Myelomonocytic Leukemia (CMML)
- Refractory Anemia (RA)
- Refractory Anemia with Excess Blasts (RAEB)
- Refractory Anemia with Excess Blasts in Transformation (RAEB-T)
- Refractory Anemia with Ringed Sideroblasts (RARS)
Myeloproliferative Disorders
- Acute Myelofibrosis
- Agnogenic Myeloid Metaplasia (Myelofibrosis)
- Essential Thrombocythemia
- Polycythemia Vera
Stem Cell Disorders
- Aplastic Anemia (Severe)
- Congenital Cytopenia
- Dyskeratosis Congenita
- Fanconi Anemia
- Paroxysmal Nocturanal Hemoglobinuria (PHN)
- Pure Red cell Aplasia
Inherited Platelet Abnormalities
- Amegakaryocytosis / Congenital Thrombocytopenia
Plasma Cell Disorders
- Multiple Myeloma
- Plasma Cell Leukemia
- Waldenstrom's Macroglobulinemia
Other Malignancies
- Brain Tumors
- Breast Cancer
- Ewing Sarcoma
- Neuroblastoma
- Ovarian Cancer
- Renal Cell Carcinoma
- Small-Cell Lung Cancer
- Testicular Cancer
Autoimmune Diseases
- Evan Syndrome
- Multiple Sclerosis (Experimental)
- Rheumatoid Arthritis (Experimental)
- Systemic Lupus Erythematosus (Experimental)